Maddie’s Vision partners with leading research institutes to strengthen patient and family engagement

Maddie’s Vision is proud to be partnering with several of Australia’s leading research institutions — including Murdoch Children’s Research Institute (MCRI) and the Australian National University (ANU) — as a consumer engagement collaborator on their respective Medical Research Future Fund (MRFF) projects.

At the ANU, Professor Eduardo Eyras and Associate Professor Amee George are leading the National Therapeutic mRNA Platform (NTRP), a groundbreaking initiative exploring how mRNA technology can be used to develop new treatments for Bone Marrow Failure Syndromes. To support this work, Maddie’s Vision hosted a Patient and Family Educational Session in August focused on mRNA therapies, providing the community with accessible information and gathering valuable feedback through a research survey to help shape future engagement and communication.

At MCRI, Professors Andrew Elefanty, Ed Stanley, and Associate Professor Elizabeth Ng are pioneering research to create personalised blood stem cells from a patient’s own tissue — an approach that could one day remove the need for donor transplants and the risks associated with these procedures. Their breakthrough, recently published in Nature Biotechnology, marks a major step toward safe, patient-specific therapies for Bone Marrow Failure Syndromes and leukaemia.

Maddie’s Vision has also been invited to partner on new MRFF grant applications with MCRI, the St Vincent’s Institute of Medical Research, the University of Queensland, and the Walter and Eliza Hall Institute (WEHI), reflecting growing recognition of Maddie’s Vision’s leadership in meaningful patient and family engagement.

Through these collaborations, Maddie’s Vision continues to ensure that the voice of patients and families remains at the heart of scientific progress — connecting lived experience with world-leading research to accelerate hope and impact for those affected by Bone Marrow Failure Syndromes.