Projects
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Outcomes of Haematopoietic Stem Cell Transplantation for Paediatric Patients with Severe Aplastic Anaemia (SAA) and Bone Marrow Failure (BMF) Syndromes.

2021-2022 (Grant-in-Aid): Outcomes of Haematopoietic Stem Cell Transplantation for Paediatric Patients with Severe Aplastic Anaemia (SAA) and Bone Marrow Failure (BMF) Syndromes. Dr Steven Keogh, Australasian Bone Marrow Transplant Recipient Registry (AMBTRR), St Vincent’s Hospital Sydney.

The ABMTRR has collected data on paediatric stem cell transplants since 1992. It is important the data focussed on paediatric bone marrow failure is collated and analysed to show activity and outcomes, and to then compare against international standards. This will determine best future practice to improve outcomes for patients.

This project aims to publish the transplant outcomes from the ABMTRR for Severe Aplastic Anaemia and other Bone Marrow Failure Syndromes in Australia and New Zealand in a high impact international journal so that local performance can be benchmarked against other international publications and registry data to establish an ANZ guideline for future management of these patients who come to transplant and make recommendations regarding indications for transplant.

Related Projects

Microenvironmental determinants of Aplastic Anaemia progression to MDS / AML.

2019-2021 (Grant-in-Aid): Microenvironmental determinants of Aplastic Anaemia progression to MDS / AML. Associate Professor Rachel Koldej, ACRF Translational Research Laboratory, Melbourne Health. Aplastic Anaemia is a disorder where the body ...

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Precision gene editing for the treatment of Fanconi Anaemia. 

2021-2024 (Grant-in-Aid): Precision gene editing for the treatment of Fanconi Anaemia. Dr Lorna McLeman, St Vincent’s Institute of Medical Research. Fanconi Anaemia is the most common cause of inherited bone marrow failure with a median onset of ...

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Identifying therapeutics which can be repurposed for the treatment of Myelodysplastic Syndromes and other bone marrow failure disorders.

2018-2021 (Grant-in-Aid): Identifying therapeutics which can be repurposed for the treatment of Myelodysplastic Syndromes and other bone marrow failure disorders. Associate Professor Amee George, The Australian National University. There are ...

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Using whole genome sequence analysis to find answers for unsolved cases of inherited Bone Marrow Failure Syndrome (iBMFS).

2020-2022 (Grant-in-Aid): Using whole genome sequence analysis to find answers for unsolved cases of inherited Bone marrow Failure Syndrome. Associate Professor Piers Blombery, The University of Melbourne. Inherited Bone Marrow Failure Syndromes ...

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