Outcomes of Haematopoietic Stem Cell Transplantation for Paediatric Patients with Severe Aplastic Anaemia (SAA) and Bone Marrow Failure (BMF) Syndromes.

2021-2022 (Grant-in-Aid): Outcomes of Haematopoietic Stem Cell Transplantation for Paediatric Patients with Severe Aplastic Anaemia (SAA) and Bone Marrow Failure (BMF) Syndromes. Dr Steven Keogh, Australasian Bone Marrow Transplant Recipient Registry (AMBTRR), St Vincent’s Hospital Sydney.

The ABMTRR has collected data on paediatric stem cell transplants since 1992. It is important the data focussed on paediatric bone marrow failure is collated and analysed to show activity and outcomes, and to then compare against international standards. This will determine best future practice to improve outcomes for patients.

This project aims to publish the transplant outcomes from the ABMTRR for Severe Aplastic Anaemia and other Bone Marrow Failure Syndromes in Australia and New Zealand in a high impact international journal so that local performance can be benchmarked against other international publications and registry data to establish an ANZ guideline for future management of these patients who come to transplant and make recommendations regarding indications for transplant.